One patient in the experiment died two months after receiving the experimental therapy, but the researchers did not report the death to the agency.
Should I join a clinical trial for an experimental therapy?
Doctors report that the experimental therapy, when given over two years, seems to produce a major reduction in the disease's progression.
The four-year response is longer than any achieved with other experimental therapies, scientists said.
He met with researchers, demanding whatever experimental therapies they were pursuing.
The experimental therapy is so promising that the scientists plan to begin treating next month another girl who has the disease.
"Finally we've recognized that you need a source of sufficient funding for experimental therapy."
Under the experimental therapy, the man's arthritis has markedly improved.
But her insurer, like many around the country, said it would not cover an experimental therapy.
The latest try at a new experimental therapy had failed.